5 trends tracked about this subject — the full history, oldest to newest below.
MeiraGTx has secured significant new funding from Oberland Capital to advance two gene therapies toward commercialization.
The FDA's top gene therapy regulator is stepping down, amid a significant setback for a kidney disease drug.
A Louisiana man is the first in the state to be functionally cured of sickle cell disease.
The FDA is reversing its rejection of Regenxbio's gene therapy for Hunter syndrome, marking the third such reversal for rare-disease drugs.
Human trials have officially commenced for the first-ever gene therapy designed to rejuvenate human cells and reverse aging.